ProQR intends to use the net proceeds from the offering, together with its existing cash and cash equivalents, to advance clinical development of its product candidates, to progress its other pipeline candidates, to advance its RNA-editing technology platforms, and for working capital and other general corporate purposes.

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Key updates At ARVO ProQR will present additional positive pre-clinical proof-of-concept data for QR-110 targeting LCA 10. The company has recently received IND clearance to start clinical | January 11, 2021 ProQR plans to independently advance its pipeline of RNA medicines to establish a multi-product, platform company in IRD. By 2023, the company expects its pipeline to have at least two commercial products, and at least three late-stage and seven early-stage programs in development. Proven leader with deep worldwide ophthalmology experience, including multiple approvals globallyLEIDEN, Netherlands & CAMBRIDGE, Mass., Oct. 05, 2020 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V 2016-03-01 · ProQR to Highlight a Growing Pipeline During a Research & Development Day and Present at the Barclays Global Healthcare Conference March 01, 2016 07:00 ET | Source: ProQR Therapeutics N.V. ProQR LEIDEN, Netherlands & CAMBRIDGE, Mass., April 02, 2021 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (Nasdaq:PRQR), a company dedicated to changing lives through the creation of transformative RNA ProQR Therapeutics N.V. Investor Contact: Sarah Kiely ProQR Therapeutics N.V. T: +1 617 599 6228 skiely@proqr.com or Hans Vitzthum LifeSci Advisors T: +1 617 535 7743 hans@lifesciadvisors.com ProQR Therapeutics N.V. (Nasdaq: PRQR) shares rallied to close up 62% to $9.22, after initially only adding 5% Wednesday following the release of data from its Phase 1/2 Stellar trial of QR-421a in adults with Usher syndrome and non-syndromic retinitis pigmentosa (nsRP). In an interview with PharmaShots, Daniel A. de Boer of ProQR shared his views on P-II/III pivotal trial of Sepofarsen to treat the root cause of a rare eye disease, Leber congenital amaurosis 10 (LCA10) Shots: The Illuminate P-II/III trial of sepofarsen is a double-masked, randomized, controlled, multiple-dose study to evaluate if sepofarsen is effective […] Jul 14, 2020 “Pontifax is pleased to enter into this strategic financing partnership with ProQR as it continues to advance its pipeline of RNA therapies for  ophthalmology candidates in our pipeline, as we believe that RNA oligonucleotides hold great promise for the treatment of a variety of genetic eye diseases.”. “By acquiring the rights to QR-1123, we have strategically expanded our pipeline in retinal diseases.

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“Since last year we have made good progress on executing on our strategy to develop life-changing therapies for patients in need, through a diversified pipeline with a balanced risk profile,” said Daniel A. de Boer, CEO of ProQR. Learn more about our Pipeline of RNA therapies. Patient-focused drug development In order to achieve our goals, ProQR strives to integrate the patient voice into our decision-making throughout the drug development process as we believe that a patient-focused strategy is crucial to our success. PRQR boasts a pipeline of 18 drug candidates, nearly all in early-stage development.

ProQR’s pipeline now includes two clinical programs, one preclinical program and two programs ready to enter development. “Since last year we have made good progress on executing on our strategy to develop life-changing therapies for patients in need, through a diversified pipeline with a balanced risk profile,” said Daniel A. de Boer, CEO of ProQR.

Charles Gross , Benzinga Staff Writer 19 Sep 2017 Our goal for this disease is to develop a pipeline of programs that can treat DEB mutations in a targeted manner and to actively advance the  6 Feb 2020 As a partner of the program ProQR has access to expert physicians and pipeline with patients and their loved ones in mind. www.proqr.com.

We are ProQR. About us; Vision 2023; Leadership; Careers; Contact; Science & Pipeline. Research and development pipeline; Clinical Trials. QR-1123 Aurora phase 1/2 study for adRP; Sepofarsen ILLUMINATE phase 2/3 study for LCA10; QR-421a STELLAR phase 1/2 study for Usher syndrome; Sepofarsen INSIGHT – phase 1b/2 study for LCA10; Sepofarsen

In the trial, QR-421a demonstrated benefit on multiple measures of vision that moved in concordance, including visual acuity, visual fields, and optical coherence tomography (OCT We are ProQR Therapeutics, a biotech company based in Leiden, the Netherlands and Cambridge, MA. We develop RNA therapies for inherited retinal diseases, with a high need for new medicines. The vast m. Leiden. 3 Tracks. 3 Followers. Stream Tracks and Playlists from ProQR … 2020-03-31 Agenda Overview and introduction by Daniel de Boer The relevance of the Nasal Potential Difference test in CF by JP Clancy, M.D. Results of the QR-010 NPD study by Noreen Henig, M.D. Pipeline and path ahead by Daniel de Boer Q&A session with JP Clancy, M.D., Noreen Henig, M.D., Smital Shah and Daniel de Boer ProQR Therapeutics 2 R&D pipeline RNA therapies for rare genetic diseases At ProQR we develop antisense oligonucleotides, or RNA therapies, to treat genetic diseases that are rare.

“Since last year we have made good progress on executing on our strategy to develop life-changing therapies for patients in need, through a diversified pipeline with a balanced risk profile,” said Daniel A. de Boer, CEO of ProQR. Learn more about our Pipeline of RNA therapies. Patient-focused drug development In order to achieve our goals, ProQR strives to integrate the patient voice into our decision-making throughout the drug development process as we believe that a patient-focused strategy is crucial to our success. ProQR is a clinical stage biotech company that discovers and develops unique RNA therapies for severe genetic disorders, specialized in retinal diseases.
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Learn more  Mar 12, 2018 ProQR's first program, now the most advanced in its pipeline, is an RNA oligonucleotide that targets the cystic fibrosis gene CFTR. ProQR Therapeutics N.V. (Nasdaq:PRQR), a company dedicated to changing RNA repair platform technologies we are growing our pipeline with patients and  6 days ago ProQR Therapeutics is dedicated to changing lives through the creation of we are growing our pipeline with patients and loved ones in mind. News.

Cash runway to last through to 2021 following recent public offering. ProQR was founded in 2012 by CEO Daniel de Boer and co-founders Henri Termeer, Dinko Valerio and Gerard Platenburg. The company’s current pipeline includes potential treatments for rare genetic diseases including Leber's congenital amaurosis, (LCA10) dystrophic epidermolysis bullosa and Usher syndrome. 2019-03-13 · The therapies in the ProQR pipeline utilize an RNA oligonucleotide technology platform to repair genetic defects, targeting significant parts of the mutations that are known causes of inherited ProQR intends to use the net proceeds from the offering, together with its existing cash and cash equivalents, to advance clinical development of its product candidates, to progress its other pipeline candidates, to advance its RNA-editing technology platforms, and for working capital and other general corporate purposes.
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ProQR Therapeutics is developing RNA-based therapeutics for the treatment of genetic QRX 203 is undergoing early research development (ProQR pipeline,  

The company is expected to present Phase I/II interim data in the first quarter of 2019. With March newly here, the company is approaching the timeline that they set out. “We are pleased to see QR-421a advancing to pivotal testing and proud to support the work of ProQR as they advance their pipeline of RNA therapies to potentially help children, adults, and families who are affected by blindness caused by USH2A mutations and other rare inherited retinal diseases.” Phase 1/2 Stellar trial of QR-421a Upcoming Data and Focus. QR-313 is the short term catalyst amongst many that ProQR has in their pipeline. The company is expected to present Phase I/II interim data in the first quarter of 2019. With March newly here, the company is approaching the timeline that they set out. 2021-03-31 ProQR R&D day Highlights Progress on Pipeline and Introduces Axiomer®, a novel proprietary RNA Technology ProQR to host an R&D day in New York today, June … Learn more about ProQR at www.proqr.com.

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Research and development pipeline; Clinical Trials.

RNA technology to benefit patients. At ProQR science is literally at the heart of what we do. The offices at our headquarters in Leiden are centered around the laboratories where our scientists discover and test our novel RNA therapies. ProQR’s pipeline now includes two clinical programs, one preclinical program and two programs ready to enter development. “Since last year we have made good progress on executing on our strategy to develop life-changing therapies for patients in need, through a diversified pipeline with a balanced risk profile,” said Daniel A. de Boer, CEO of ProQR. Learn more about our Pipeline of RNA therapies.